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Glorieux, F. H., Langdahl, B., Chapurlat, R., De Beur, S. J., Sutton, V. R., Poole, K. E. S., Dahir, K. M., Orwoll, E. S., Willie, B. M., Mikolajewicz, N., Zimmermann, E., Hosseinitabatabaei, S., Ominsky, M. S., Saville, C., Clancy, J., Mackinnon, A., Mistry, A. & Javaid, M. K. (2024). Setrusumab for the treatment of osteogenesis imperfecta: 12-month results from the phase 2b asteroid study. Journal of Bone and Mineral Research (JBMR), 39(9), 1215-1228. https://doi.org/10.1093/jbmr/zjae112
Elitzur, S., Shiloh, R., Loeffen, J. L. C., Pastorczak, A., Takagi, M., Bomken, S., Baruchel, A., Lehrnbecher, T., Tasian, S. K., Abla, O., Arad-Cohen, N., Astigarraga, I., Ben-Harosh, M., Bodmer, N., Brozou, T., Ceppi, F., Chugaeva, L., Dalla Pozza, L., Ducassou, S. ... Borkhardt, A. (2024). ATM germ line pathogenic variants affect outcomes in children with ataxia-telangiectasia and hematological malignancies. Blood, 144(11), 1193-1205. https://doi.org/10.1182/blood.2024024283
Kristensen, D. T., Øvlisen, A. K., Jakobsen, L. H. K., Severinsen, M. T., Hannig, L. H., Starklint, J., Hilsøe, M. H., Vallentin, A. P., Brabrand, M., Hasselbalch, H. C., El-Galaly, T. C. & Roug, A. S. (2024). Metformin use and risk of myeloproliferative neoplasms: a Danish population–based case-control study. Blood Advances, 8(16), 4478-4485. https://doi.org/10.1182/bloodadvances.2023012266
Lønborg, J., Jabbari, R., Sabbah, M., Veien, K. T., Niemelä, M., Freeman, P., Linder, R., Ioanes, D., Terkelsen, C. J., Kajander, O. A., Koul, S., Savontaus, M., Karjalainen, P., Erglis, A., Minkkinen, M., Sørensen, R., Tilsted, H.-H., Holmvang, L., Bieliauskas, G. ... NOTION-3 Study Group (2024). PCI in Patients Undergoing Transcatheter Aortic-Valve Implantation. The New England Journal of Medicine, 391(23), 2189-2200. https://doi.org/10.1056/NEJMoa2401513